NDA/BLA filedconf 0.75
ux111 — NDA/BLA filed
$RARE · Ultragenyx Pharmaceutical Inc. · Sanfilippo syndrome Type A (MPS IIIA)
Event date
Date TBD
Sponsor runway
3 mo
$175.0M liquid
Evidence
Comparable historical nda/bla fileds· last 5 years · same event type
| Ticker | Drug | Date | Outcome |
|---|---|---|---|
| $AXSM | — | 2025-12-31 | unknown |
| $RCKT | kresladi | 2025-10-14 | unknown |
| $ALDX | reproxalap | 2025-07-17 | unknown |
| $ETON | et-600 | 2025-07-08 | unknown |
| $BCRX | orladeyo (berotralstat) | 2025-05-14 | unknown |
| $CORT | relacorilant | 2025-03-03 | unknown |
| $ALDX | reproxalap | 2024-11-01 | unknown |
| $AXSM | axs-07 | 2024-09-04 | unknown |
| $RCKT | kresladi | 2023-10-02 | unknown |
| $GERN | imetelstat | 2023-08-21 | unknown |
Recent insider activity· ±90 days
9 insiders · 0 buys · 3 sells
Sell10b5-1
2026-05-18SULIMAN SHEHNAAZ
Director
5,740 @ $25.12$144K
Grant
2026-05-14Dunsire Deborah
Director
14,058 @ ——
Grant
2026-05-14Sanders Corazon (Corsee) D.
Director
7,751 @ ——
Grant
2026-05-14Sanders Corazon (Corsee) D.
Director
14,058 @ ——
Grant
2026-05-14NARACHI MICHAEL
Director
7,751 @ ——
Grant
2026-05-14NARACHI MICHAEL
Director
14,058 @ ——
Grant
2026-05-14Ray Amrit
Director
7,751 @ ——
Grant
2026-05-14Ray Amrit
Director
14,058 @ ——
Grant
2026-05-14Fust Matthew K
Director
7,751 @ ——
Grant
2026-05-14Fust Matthew K
Director
14,058 @ ——
Grant
2026-05-14Dunsire Deborah
Director
7,751 @ ——
Grant
2026-05-14WELCH DANIEL G
Director
7,751 @ ——
Grant
2026-05-14WELCH DANIEL G
Director
14,058 @ ——
Grant10b5-1
2026-05-14SULIMAN SHEHNAAZ
Director
7,751 @ ——
Grant10b5-1
2026-05-14SULIMAN SHEHNAAZ
Director
14,058 @ ——
Sell
2026-05-05Crombez Eric
EVP and Chief Medical Officer
344 @ $24.96$9K
Sell10b5-1
2026-05-01Horn Howard
Chief Financial Officer
4,683 @ $24.90$117K