PDUFAconf 0.99
zilganersen — PDUFA
$IONS · IONIS PHARMACEUTICALS INC · Alexander disease (AxD)
Event date
September 22, 2026
in 108 days
Sponsor runway
7 mo
$1.92B liquid
Evidence
Comparable historical pdufas· last 5 years · same event type
75% hit rate (3/4)
| Ticker | Drug | Date | Outcome |
|---|---|---|---|
| $RCKT | kresladi | 2026-03-28 | success |
| $RYTM | imcivree | 2026-03-20 | success |
| $CYTK | aficamten | 2025-12-26 | unknown |
| $ALDX | reproxalap | 2025-12-16 | unknown |
| $BCRX | orladeyo | 2025-12-12 | success |
| $OMER | narsoplimab | 2025-09-25 | unknown |
| $BCRX | orladeyo (berotralstat) | 2025-09-12 | unknown |
| $ETON | et-400 | 2025-05-28 | unknown |
| $ALDX | reproxalap | 2025-04-02 | failure |
| $IONS | olezarsen | 2024-12-19 | unknown |