mozafancogene autotemcel — NDA/BLA filed

“On October 3, 2025, Rocket Pharmaceuticals, Inc. ("Rocket" or the "Company") reported that it has voluntarily withdrawn its Biologics License Application ("BLA") to the U.S. Food and Drug Administration ("FDA") for mozafancogene autotemcel (also known as "Fanskya," "Fanca-cel," or "RP-L102"), an investigational gene therapy for the treatment of Fanconi Anemia ("FA").”